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Category: ultra-rare genetic diseases

LifeArc provides £750,000 fund for clinical trial to treat neuroferritinopathy

The progressive and incurable brain disorder currently affects approximately 100 patients worldwide

March 27, 2024 DefINe, Ferriprox, LifeArc, Lipomed, neuroferritinopathy, News, ultra-rare genetic diseases, University of Cambridge
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